Our lives were forever changed when my 9 1/2 month old great grandson William was diagnosed with a genetic disease, Spinal Muscular Atrophy (SMA). SMA is a disease that robs people of physical strength by affecting the motor nerve cells in the spinal cord, taking away the ability to walk, eat, or breathe. It is the number one genetic cause of death for infants.
This is a unique disease because no two cases are the same. We still do not know what this diagnosis means for our little William long term.
For the first time two new gene therapy treatments have been approved for SMA. One was just approved last week and it is expected to cost over 2 million dollars. This treatment can help give William a better life. His hard working parents need help with the growing costs of treatments and therapy. Will's Great Grandparents, grandparents, aunts and uncles are doing everything we can to help this little guy. We would be eternally grateful for any extra help. Love and God bless! Great Grandma Denese