Help raise money to cure my disability.

Hi, my name is Sophie, and I have a progressive genetic disability called Spinal Muscular Atrophy (or SMA for short), type 2. I've been in a wheelchair since I was 18 months old. I can't move my legs, have very limited use of my arms, and my breathing and swallowing are also affected; I choke a lot, and am prone to respiratory infections.

Over the years (I'm now 13), I've had around 400 hospital appointments, 100 x-rays and 7 surgeries. I pretty much spend most of my life in and out of hospital. 

Last Christmas, a drug called Spinraza was approved by the FDA. It not only stops the devastating effects of SMA, but reverses them.
If I had Spinraza, I would be able to gain back muscle strength, control of my arms my neck and the rest of my body, respiratory muscles, and I may even be able to start working on walking. I can't even begin to imagine how amazing that would be.

But, unfortunately, the cost of Spinraza if very high, and recently NICE refused to provide Spinraza on the NHS. If I don't have Spinraza soon, I will continue to deteriorate and for me every month and even every week make a huge difference.

I have dreams and ambitions like everyone else, but the rapid deterioration of my body is slowly making it impossible for me to achieve my goals.

Treatment shouldn't cost thousands. Please help me raise money, so I can gain access to Spinraza, so I can fulfil my life's potential.