<div><strong>Paxton's Story: A Rare Genetic Battle</strong>
</div>
<div><br />
</div>
<div>Our son Paxton, recently diagnosed with an ultra-rare genetic mutation on the CLCN6 gene, faces immense challenges including Autism Spectrum Disorder, severe epilepsy, hypotonia, and poor motor coordination. <strong>This mutation is neurodegenerative, meaning time is critical.</strong>
</div>
<div><br />
</div><img alt="" media_type="3" src="https://d2g8igdw686xgo.cloudfront.net/81595459_1723662021665499_r.jpeg" width="100%" />
<div><br />
</div>
<div><strong>The Urgency of Paxton's Condition</strong>
</div>
<div><br />
</div>
<div>Paxton is one of only a handful of known cases worldwide, and currently, no research exists for a gene therapy due to the small patient population. <strong>However, we have a unique opportunity to develop a life-saving treatment for Paxton at the University of Massachusetts' Horae Gene Therapy Center.</strong>
</div>
<div><br />
</div><img alt="" media_type="3" src="https://d2g8igdw686xgo.cloudfront.net/81595459_1723662535890642_r.jpeg" width="100%" />
<div><br />
</div>
<div><strong>Why We Need Your Help</strong>
</div>
<div><br />
</div>
<div>The scientists will create a custom gene therapy using specialized viruses called Adeno-Associated Viruses (AAV). <strong>The entire process, including studying the mutation in laboratory models, developing and testing the therapy, and administering it to Paxton, will take approximately three years and cost $1.5 million.</strong>
</div>
<div><br />
</div><img alt="" media_type="3" src="https://d2g8igdw686xgo.cloudfront.net/81595459_1723662981287071_r.jpeg" width="100%" />
<div><br />
</div>
<div><strong>The Science Behind the Therapy</strong>
</div>
<div><br />
</div>
<div>The University of Massachusetts' Horae Gene Therapy Center will develop, test and deliver a gene therapy for Paxton through a clinical trial. <strong>This therapy involves using specially designed viruses to replace the faulty gene with a functional one. </strong>
</div>
<div><br />
</div>
<div><strong>Funding Breakdown and Timeline</strong>
</div>
<div><br />
</div>
<div><strong>We need to raise these funds urgently to give Paxton the chance he deserves.</strong> Your support will directly fund the development of this crucial gene therapy. <strong>Time is against us, but with your help, we can make this happen.</strong>
</div>
<div><br />
</div><img alt="" media_type="3" src="https://d2g8igdw686xgo.cloudfront.net/81595459_1723663320491989_r.jpeg" width="100%" />
<div><br />
</div>
<div><strong>How You Can Make a Difference</strong>
</div>
<div><br />
</div>
<div>From the depths of our hearts, thank you to everyone who reads Paxton's story and donates. Please share our campaign to reach as many people as possible. <strong>Every dollar counts towards saving our son's life.</strong>
</div>
<div><br />
</div>
<div><strong>Follow Paxton's Journey</strong>
</div>
<div><br />
</div>
<div>Follow our journey and get updates through our website and YouTube channel. More social media links will be available soon.
</div>
<div><br />
</div>
<div>Website: <a href="https://www.cureclcn6.org" target="_blank" rel="noreferrer noopener"><a href="https://www.cureclcn6.org" target="_blank" class="" rel="nofollow noopener noreferrer">https://www.cureclcn6.org</a></a>
</div>
<div>YouTube Channel: <a href="https://www.youtube.com/" target="_blank" rel="noreferrer noopener"><a href="http://www.youtube.com/" target="_blank" class="" rel="nofollow noopener noreferrer">http://www.youtube.com/</a></a>@CureCLCN6
</div>
<div>On Facebook, Instagram and TikTok follow Paxton's Pioneers
</div>
<div><br />
</div><img alt="" media_type="3" src="https://d2g8igdw686xgo.cloudfront.net/81595459_1723663860185529_r.jpeg" width="100%" />
<div><br />
</div>
<div><strong>Heartfelt Thanks and How to Share</strong>
</div>
<div><br />
</div>
<div>F<strong>rom the bottom of our hearts, thank you to everyone who has read this story and has donated to help our son. Please share our story with others to help us reach a wider audience and to reach our goal.</strong> 100% of all donations will go towards developing, testing and administering the gene therapy.
</div>
<div><br />
</div><img alt="" media_type="3" src="https://d2g8igdw686xgo.cloudfront.net/81595459_1723664060410471_r.jpeg" width="100%" />
<div><br />
</div>
<div><br />
</div>
<div>Cure CLCN6, Inc., is a registered non-profit organization in the state of California. Cure CLCN6 Inc., has applied for 501(c)3 tax exempt status with the Internal Revenue Service (IRS) and the application is pending. Upon approval, all donations will be tax deductible dating back to February 2024.
</div>

Anonymous

Cash Donations 

Barbara Colangione

Menchie Adkinson

Help Save Paxton's Life: A Rare Genetic Battle

Il reste encore $1,265,316. Aidez-nous à créer une dynamique.